Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets

Fatty acid binding proteins (FABPs) are small intracellular proteins that reversibly bind fatty acids and other hydrophobic ligands. In cestodes, due to their inability to synthesise fatty acids and cholesterol de novo, FABPs, together with other lipid binding proteins, have been proposed as essenti...

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Autores principales: Bélgamo, Julián Alberto, Alberca, Lucas Nicolás, Pórfido, Jorge Luis, Caram Romero, Franco Nahuel, Rodríguez, Santiago, Talevi, Alan, Córsico, Betina, Franchini, Gisela Raquel
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Publicado: 2020
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Acceso en línea:http://sedici.unlp.edu.ar/handle/10915/136766
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spelling I19-R120-10915-1367662023-11-08T14:15:35Z http://sedici.unlp.edu.ar/handle/10915/136766 Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets Bélgamo, Julián Alberto Alberca, Lucas Nicolás Pórfido, Jorge Luis Caram Romero, Franco Nahuel Rodríguez, Santiago Talevi, Alan Córsico, Betina Franchini, Gisela Raquel 2020 2022-05-23T19:05:59Z en Bioquímica Drug repurposing Target repurposing FABP Echinococcus spp Virtual screening Neglected tropical diseases Fatty acid binding proteins (FABPs) are small intracellular proteins that reversibly bind fatty acids and other hydrophobic ligands. In cestodes, due to their inability to synthesise fatty acids and cholesterol de novo, FABPs, together with other lipid binding proteins, have been proposed as essential, involved in the trafficking and delivery of such lipophilic metabolites. Pharmacological agents that modify specific parasite FABP function may provide control of lipid signalling pathways, inflammatory responses and metabolic regulation that could be of crucial importance for the parasite development and survival. Echinococcus multilocularis and Echinococcus granulosus are, respectively, the causative agents of alveolar and cystic echinococcosis (or hydatidosis). These diseases are included in the World Health Organization's list of priority neglected tropical diseases. Here, we explore the potential of FABPs from cestodes as drug targets. To this end, we have applied a target repurposing approach to identify novel inhibitors of Echinococcus spp. FABPs. An ensemble of computational models was developed and applied in a virtual screening campaign of DrugBank library. 21 hits belonging to the applicability domain of the ensemble models were identified, and 3 of the hits were assayed against purified E. multilocularis FABP, experimentally confirming the model's predictions. Noteworthy, this is to our best knowledge the first report on isolation and purification of such four FABP, for which initial structural and functional characterization is reported here. Instituto de Investigaciones Bioquímicas de La Plata Laboratorio de Investigación y Desarrollo de Bioactivos Articulo Articulo http://creativecommons.org/licenses/by-nc-sa/4.0/ Creative Commons Attribution-NonCommercial-ShareAlike 4.0 International (CC BY-NC-SA 4.0) application/pdf 1275-1288
institution Universidad Nacional de La Plata
institution_str I-19
repository_str R-120
collection SEDICI (UNLP)
language Inglés
topic Bioquímica
Drug repurposing
Target repurposing
FABP
Echinococcus spp
Virtual screening
Neglected tropical diseases
spellingShingle Bioquímica
Drug repurposing
Target repurposing
FABP
Echinococcus spp
Virtual screening
Neglected tropical diseases
Bélgamo, Julián Alberto
Alberca, Lucas Nicolás
Pórfido, Jorge Luis
Caram Romero, Franco Nahuel
Rodríguez, Santiago
Talevi, Alan
Córsico, Betina
Franchini, Gisela Raquel
Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
topic_facet Bioquímica
Drug repurposing
Target repurposing
FABP
Echinococcus spp
Virtual screening
Neglected tropical diseases
description Fatty acid binding proteins (FABPs) are small intracellular proteins that reversibly bind fatty acids and other hydrophobic ligands. In cestodes, due to their inability to synthesise fatty acids and cholesterol de novo, FABPs, together with other lipid binding proteins, have been proposed as essential, involved in the trafficking and delivery of such lipophilic metabolites. Pharmacological agents that modify specific parasite FABP function may provide control of lipid signalling pathways, inflammatory responses and metabolic regulation that could be of crucial importance for the parasite development and survival. Echinococcus multilocularis and Echinococcus granulosus are, respectively, the causative agents of alveolar and cystic echinococcosis (or hydatidosis). These diseases are included in the World Health Organization's list of priority neglected tropical diseases. Here, we explore the potential of FABPs from cestodes as drug targets. To this end, we have applied a target repurposing approach to identify novel inhibitors of Echinococcus spp. FABPs. An ensemble of computational models was developed and applied in a virtual screening campaign of DrugBank library. 21 hits belonging to the applicability domain of the ensemble models were identified, and 3 of the hits were assayed against purified E. multilocularis FABP, experimentally confirming the model's predictions. Noteworthy, this is to our best knowledge the first report on isolation and purification of such four FABP, for which initial structural and functional characterization is reported here.
format Articulo
Articulo
author Bélgamo, Julián Alberto
Alberca, Lucas Nicolás
Pórfido, Jorge Luis
Caram Romero, Franco Nahuel
Rodríguez, Santiago
Talevi, Alan
Córsico, Betina
Franchini, Gisela Raquel
author_facet Bélgamo, Julián Alberto
Alberca, Lucas Nicolás
Pórfido, Jorge Luis
Caram Romero, Franco Nahuel
Rodríguez, Santiago
Talevi, Alan
Córsico, Betina
Franchini, Gisela Raquel
author_sort Bélgamo, Julián Alberto
title Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
title_short Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
title_full Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
title_fullStr Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
title_full_unstemmed Application of target repositioning and in silico screening to exploit fatty acid binding proteins (FABPs) from Echinococcus multilocularis as possible drug targets
title_sort application of target repositioning and in silico screening to exploit fatty acid binding proteins (fabps) from echinococcus multilocularis as possible drug targets
publishDate 2020
url http://sedici.unlp.edu.ar/handle/10915/136766
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